Related by context. All words. (Click for frequent words.) 75 Duchenne muscular dystrophy 71 Duchenne 71 Duchenne Muscular Dystrophy DMD 68 Spinal Muscular Atrophy 67 Cystic Fibrosis 67 muscular dystrophy 66 Spinal Muscular Atrophy SMA 65 Duchenne muscular dystrophy DMD 65 cystic fibrosis 64 Friedreich ataxia 64 Muscular Dystrophy 64 Friedreich Ataxia 64 spinal muscular atrophy SMA 64 Huntington Disease 62 Multiple Sclerosis 61 juvenile diabetes 61 Juvenile Diabetes 61 Angelman Syndrome 61 ALS Amyotrophic Lateral Sclerosis 60 Rett Syndrome 60 cystinosis 60 neuromuscular disease 60 Polycystic Kidney Disease 60 Batten Disease 59 neurofibromatosis 59 Scleroderma 59 spinal muscular atrophy 59 Neuroblastoma 59 Tuberous Sclerosis 59 Mitochondrial Disease 59 Leber Congenital Amaurosis LCA 59 cystic fibrosis CF 59 Osteosarcoma 59 neuroblastoma 59 Leukodystrophy 58 Leukemia 58 Juvenile Arthritis 58 Cystinosis 58 Cystic Fibrosis CF 58 Pompe Disease 58 ALS 58 Retinitis Pigmentosa RP 58 MPS VI 58 Ewing Sarcoma 58 Neurofibromatosis 58 Muscular dystrophy 57 Progeria 57 Lupus 57 Leber congenital amaurosis 57 DIPG 57 leukemia 57 degenerative disorder 57 limb girdle muscular dystrophy 57 Parkinson Disease 57 Nephrotic Syndrome 57 Pompe disease 57 carcinoid cancer 57 Pancreatic Cancer 57 Rett syndrome 57 Barth Syndrome 57 Niemann Pick 56 acute myeloid leukemia 56 Acute Myelogenous Leukemia 56 Sanfilippo Syndrome 56 leukodystrophies 56 amyotrophic lateral sclerosis ALS 56 Rhabdomyosarcoma 56 Leber Congenital Amaurosis 56 Duchene Muscular Dystrophy 56 Fragile X Syndrome 56 Hodgkin Lymphoma 56 Canavan Disease 56 Retinoblastoma 56 hypophosphatasia 56 Pompe 56 Pompe disease rare 56 genetic disorder 56 NF2 56 Juvenile Rheumatoid Arthritis 56 Ataxia 56 Crohn Disease 55 Acute Myelogenous Leukemia AML 55 Sarcoma 55 lupus 55 Amyotrophic Lateral Sclerosis ALS 55 Duchene muscular dystrophy 55 Fanconi anemia 55 Acute Lymphoblastic Leukemia 55 Niemann Pick disease 55 Usher Syndrome 55 Acute Myeloid Leukemia 55 Lymphoma 55 multiple sclerosis 55 lymphoblastic leukemia 55 Progeria Research 55 fatal neuromuscular disorder 55 Krabbe Disease 55 histiocytosis 55 leukemia ALL 55 Fragile X 54 Becker muscular dystrophy 54 scleroderma 54 Burkitt Lymphoma 54 Niemann Pick Disease 54 Sickle Cell Anemia 54 Duchenne Becker 54 Chronic Lymphocytic Leukemia 54 progeria 54 Hemophilia B 54 Ewing sarcoma 54 Fanconi Anemia 54 Aplastic Anemia 54 Ewings Sarcoma 54 Dystrophy 54 rhabdomyosarcoma 54 Merkel Cell Carcinoma 54 Leukemia Lymphoma 54 mitochondrial disease 54 Severe Primary IGFD 54 Acute Leukemia 53 motor neuron disease 53 Wilms Tumor 53 sarcoma 53 Lou Gehrigs disease 53 Melanoma 53 Sanfilippo syndrome 53 Diamond Blackfan Anemia 53 Myeloma 53 degenerative neurological disorder 53 Lafora disease 53 Crohn disease 53 Multiple Myeloma 53 congenital muscular dystrophy 53 epilepsy 53 myotonic muscular dystrophy 53 Dystonia 53 Glioblastoma 53 muscle wasting 53 Primary Immune Deficiency 53 ependymoma 53 cancer 53 Multiple Sclerosis MS 53 DMD 53 Non Hodgkin Lymphoma 53 acute lymphoblastic leukemia 52 Medulloblastoma 52 Lou Gehrig Disease 52 Alzheimer Disease 52 Epilepsy 52 Brain Tumour 52 Burkitt lymphoma 52 multiple sclerosis MS 52 retinoblastoma 52 myasthenia gravis 52 Cardiomyopathy 52 Fragile X syndrome 52 Restless Legs Syndrome 52 dyskeratosis congenita 52 Pulmonary Fibrosis 52 Parkinsons Disease 52 autoimmune disease 52 Ectodermal Dysplasia 52 Leukaemia 52 inherited neurodegenerative disorder 52 adrenoleukodystrophy ALD 52 Rare Disease 52 hepatoblastoma 52 Epstein Barr Virus 52 Motor Neurone Disease 52 Alport Syndrome 52 Parkinson disease 52 Battens Disease 52 Sudden Arrhythmia Death 52 tuberous sclerosis complex 52 Parkinsons 52 Sickle Cell Disease 52 Alopecia Areata 52 multiple myeloma 52 mitochondrial myopathy 52 Leber congenital amaurosis LCA 52 Motor Neuron 52 neurofibromatosis NF 52 Acute Lymphoblastic Leukaemia 52 Hurler syndrome 52 Inflammatory Breast Cancer 51 Adrenoleukodystrophy 51 Diabetes 51 1 Antitrypsin Deficiency 51 disease 51 polycystic kidney disease 51 lymphoblastic lymphoma 51 MELAS 51 Adenoid Cystic Carcinoma 51 medulloblastoma 51 Marfan Syndrome 51 Myasthenia Gravis 51 degenerative neurological disease 51 Transverse Myelitis 51 Lou Gherig disease 51 Alzheimer disease AD 51 Lateral Sclerosis 51 Moebius Syndrome 51 Amyloidosis 51 Stargardt disease 51 sickle cell disease 51 LHON 51 Chronic Myeloid Leukemia 51 Hodgkins lymphoma 51 Alzhiemer 51 neurodegenerative disorder 51 Spina Bifida 51 Progressive Supranuclear Palsy 51 Histiocytosis 51 juvenile myelomonocytic leukemia 51 neurodegenerative disease 51 Acute Myeloid Leukemia AML 51 Diffuse Intrinsic Pontine Glioma 51 Macular Degeneration 51 haemophilia 51 Glioblastoma Multiforme 51 progressive neurodegenerative disorder 51 Age Related Macular 51 Cystic fibrosis 51 chronic granulomatous disease 51 Friedrich Ataxia 51 sickle cell anemia 51 wet macular degeneration 51 ectodermal dysplasia 51 Dravet Syndrome 51 Exon Skipping 51 Alzeimer 51 Gaucher Disease 51 CureDuchenne 51 pediatric brain tumor 51 facioscapulohumeral muscular dystrophy 51 Hemochromatosis 51 Krabbe Leukodystrophy 51 fatal neurodegenerative disorder 51 Glioma 51 Hutchinson Gilford Progeria Syndrome 51 Rheumatoid Arthritis 51 lysosomal storage diseases 50 Crohn 50 Wiskott Aldrich Syndrome 50 Brain Tumor 50 Stargardt Disease 50 debilitating autoimmune 50 diffuse intrinsic pontine glioma 50 PKD Foundation 50 leukemia AML 50 retinal degenerative disease 50 inflammatory arthritis 50 aplastic anemia 50 NephCure Foundation 50 neuromuscular disorder 50 Chronic lymphocytic leukemia 50 Myocarditis 50 Dravet syndrome 50 AAT deficiency 50 Immune Thrombocytopenic Purpura 50 Mucopolysaccharidosis 50 hereditary spastic paraplegia 50 Non Hodgkins Lymphoma 50 Myelodysplastic Syndrome 50 systemic lupus erythematosus 50 myotonic dystrophy 50 idiopathic pulmonary fibrosis IPF 50 Sudden Unexplained Death 50 FSHD 50 Haemophilia 50 Acute Myeloid Leukaemia 50 Fibrosis 50 Maroteaux Lamy syndrome 50 motor neuron diseases 50 JDRF 50 relapsed leukemia 50 inherited neurological disorder 50 Lewy Body Dementia 50 Cystic Fibrosis Foundation 50 Leber Hereditary Optic Neuropathy 50 Psoriasis 50 Immune Thrombocytopenic Purpura ITP 50 Alzheimers disease 50 DebRA 50 Prostrate Cancer 50 Stargardt Macular Dystrophy 50 Malignant Melanoma 50 ankylosing spondylitis AS 50 Alzheimer 50 Cytomegalovirus 50 acute myelogenous leukemia 50 Epidermolysis Bullosa 50 embryonal rhabdomyosarcoma 50 fatal neurodegenerative 50 Syringomyelia 50 neuromuscular diseases 50 Acute Myeloid Leukaemia AML 50 osteosarcoma 50 Myasthenia gravis 50 muscular dystrophy cystic fibrosis 50 Hydrocephalus 50 Chronic Leukemia 50 Lennox Gastaut syndrome 49 ataxia telangiectasia 49 Inflammatory Bowel Disease 49 AAT Deficiency 49 Rhabdomyosarcoma rare 49 Hodgkin Disease 49 Krabbe disease 49 Brugada Syndrome 49 FSGS 49 neuro degenerative disease 49 Maroteaux Lamy Syndrome 49 PKD 49 epidermolysis bullosa EB 49 juvenile rheumatoid arthritis 49 smoldering myeloma 49 incurable genetic 49 Systemic Lupus Erythematosus 49 Morquio Syndrome 49 Amyotrophic lateral sclerosis ALS 49 Prostate Cancer 49 Lou Gerhig disease 49 Primary Immunodeficiency 49 Morquio syndrome 49 Mantle Cell Lymphoma 49 AML Leukemia 49 Ataxia Telangiectasia 49 Kidney Cancer 49 synovial sarcoma 49 Aicardi Syndrome 49 Alzheimers Disease 49 Cooley Anemia Foundation 49 Acute Lymphocytic Leukemia 49 rheumatic disease 49 MPGN 49 Action Duchenne 49 Fabry Disease 49 Crohns 49 Fragile X. 49 infantile spasms 49 Alzheimer disease 49 Tuberous Sclerosis Alliance 49 myasthenia gravis MG 49 Eosinophilic 49 DBMD 49 Ulcerative Colitis 49 Epidermolysis Bullosa EB 49 degenerative muscular 49 incurable disease 49 hemophilia 49 neuroblastoma tumor 49 inherited neurodegenerative 49 CFS ME 49 Autism 49 hereditary degenerative 49 RSRF 49 Lung Cancer 49 neuromuscular disorders 49 immunodeficiency disease 49 pediatric sarcoma 49 Acute myeloid leukemia 49 Myositis 49 Tuberous Sclerosis Complex 49 kidney disease 49 Graft Versus Host 49 Fanconi anemia FA 49 Motor Neurone 49 Uveitis 49 hemophilia B. 49 Brittle Bone 49 Hodgkins Lymphoma 49 leukodystrophy 49 AA amyloidosis 49 Hurler Syndrome 49 Hemophilia 49 motor neurone 49 Ewing sarcoma rare 49 degenerative neurological condition 49 Spinal muscular atrophy 49 fatal neuromuscular 49 rheumatoid arthritis 48 pulmonary fibrosis PF 48 Sudden Cardiac Death 48 Alzheimer Disease AD 48 PPMD 48 Charcot Marie Tooth 48 acute myelogenous leukemia AML 48 acute myelogenous 48 Retinopathy 48 1 diabetes T1D 48 alveolar rhabdomyosarcoma 48 Hereditary Disease Foundation 48 neuro degenerative disorder 48 Coeliac disease 48 retinitis pigmentosa RP 48 diabetes 48 myeloma 48 Parkinsons disease 48 Angelman syndrome 48 Cushing Syndrome 48 Myotonic dystrophy 48 mastocytosis 48 Morquio 48 Wilm Tumor 48 relapsing multiple sclerosis 48 Colitis 48 Angelman 48 neuro muscular diseases 48 lymphocytic leukemia 48 hereditary blindness 48 Aplastic Anaemia 48 cardiac channelopathies 48 acute promyelocytic leukemia 48 Austism 48 ALS Lou Gehrig 48 degenerative neuromuscular disease 48 spinocerebellar ataxia 48 Wilms Tumour 48 Waldenstrom macroglobulinemia 48 systemic scleroderma 48 ankylosing spondylitis 48 Pulmonary Hypertension 48 Myelodysplastic Syndrome MDS 48 spastic diplegia 48 Testicular Cancer 48 Autism Spectrum Disorders 48 epidermolysis bullosa 48 Breast Cancer 48 myeloproliferative neoplasms 48 Myelin Project 48 pontine glioma 48 Idiopathic Thrombocytopenic Purpura ITP 48 Cure Duchenne 48 Cholangiocarcinoma 48 chronic lymphocytic leukemia 48 SADS 48 progressive neurodegenerative disease 48 Bronchiectasis 48 acute lymphatic leukemia 48 osteosarcoma bone 48 debilitating neurological disorder 48 cerebal palsy 48 ALS amyotrophic lateral sclerosis 48 NPHP 48 Aplastic anemia 48 Lou Gherig Disease 48 Infantile Spasms 48 gynecological cancers 48 HIBM 48 discoid lupus 48 Wegener Granulomatosis 48 Lymphoma Leukemia 48 T1DM 48 Pediatric Brain Tumor 48 CHARGE syndrome 48 liver disease 48 Multiple Myeloma Research 48 retinal degenerative diseases 48 Restless Leg Syndrome 48 SNT-MC#/idebenone 48 Macula Vision Research 48 incurable neurodegenerative disease 48 lupus nephritis 48 beta thalassemia 48 Diamond Blackfan anemia 48 Proteus Syndrome 48 Pulmonary Fibrosis PF 47 Hydrocephalus Association 47 neovascular diseases 47 Amyotrophic lateral sclerosis 47 Ankylosing Spondylitis 47 Cancer 47 ceroid lipofuscinosis NCL 47 rare neurological disorder 47 Epratuzumab 47 Brain Tumor Foundation 47 hematological malignancy 47 Cockayne Syndrome 47 Von Hippel Lindau 47 Pleural Mesothelioma 47 macular degeneration 47 fronto temporal dementia 47 ataluren 47 TREAT NMD 47 psoriasis 47 Lateral Sclerosis ALS 47 progressive supranuclear palsy 47 Cancer Research 47 hereditary disorder 47 neurofibromatosis type 47 Arthritis 47 severe aplastic anemia 47 Ovarian Cancer 47 Juvenile Diabetes Research 47 Bleeding Disorder 47 Angelman Syndrome Foundation 47 incurable neurological disorder 47 Myelodysplastic Syndromes MDS 47 amyotrophic lateral sclerosis 47 Acute Promyelocytic Leukemia 47 Lyme Disease 47 idiopathic thrombocytopenic purpura ITP 47 Arteriosclerosis 47 Chronic Obstructive Pulmonary 47 Childhood Cancer 47 leukemia CLL 47 MJFF 47 hemophagocytic lymphohistiocytosis 47 TTR amyloidosis 47 Von Willebrand disease 47 Juvenile Idiopathic Arthritis 47 mitochondrial diseases 47 Kawasaki Disease 47 cerebral palsy 47 Ichthyosis 47 dystonia 47 degenerative disease 47 Acute Respiratory Failure 47 neurogenic orthostatic hypotension 47 Hodgkins Disease 47 medulloblastomas 47 neuroendocrine tumors 47 retinal diseases 47 Syndrome SADS 47 Parkinson disease PD 47 spina bifida 47 alzheimer disease 47 Tourette syndrome 47 corneal blindness 47 Langerhans cell histiocytosis 47 NephCure 47 Lafora 47 neurological disorder 47 Leukemias 47 Keratoconus 47 Pemphigus 47 ALS Therapy 47 autoimmune uveitis 47 CIDP 47 Hypertrophic Cardiomyopathy HCM 47 myelofibrosis 47 Prader Willi Syndrome 47 glioblastoma 47 urological cancers 47 adrenoleukodystrophy 47 metachromatic leukodystrophy 47 Pancreatic 47 Myopathy 47 sarcomas 47 metabolic disorder 47 severe oral mucositis 47 Cerebral palsy 47 systemic lupus erythematosus SLE 47 Myotonic Muscular Dystrophy 47 primary immunodeficiencies 47 leukemia lymphoma Hodgkin 47 Philadelphia Chromosome Positive 47 Juvenile Idiopathic Arthritis JIA 47 Sickle Cell 47 spinal cord injury 47 Stomach Cancer 47 Amyotrophic Lateral Sclerosis 47 pneumococcal meningitis 47 chromosome abnormality 46 Lou Gehrig disease 46 alopecia areata 46 medulloblastoma malignant brain tumor 46 Chronic Myelogenous Leukemia 46 Hepatitis C 46 pancreatic islet cell 46 Motor Neuron Disease 46 Retinitis Pigmentosa 46 blood clotting disorder 46 Joubert Syndrome 46 Pulmonary arterial hypertension 46 osteogenesis imperfecta 46 Hutchinson Gilford Progeria 46 progeria rare 46 liver cancer 46 Polycystic kidney disease 46 DiGeorge Syndrome 46 retinitis pigmentosa 46 brain tumors 46 Langerhans Cell Histiocytosis 46 Idiopathic Pulmonary Fibrosis 46 HEADstrong Foundation 46 Rheumatoid Arthritis RA 46 Pediatric Diabetes 46 Crohns disease 46 Rubinstein Taybi syndrome 46 Porphyria 46 cystic fibrosis hereditary 46 leukemia lymphoma myeloma 46 AA Amyloidosis 46 lymphatic cancer 46 lysosomal storage disease 46 Growth Hormone Deficiency 46 osteogenic sarcoma 46 chronic myeloid leukemia 46 multisystem disease 46 haematologic malignancies 46 autoinflammatory diseases 46 inherited retinal degeneration 46 haematological cancers 46 genetic disorders 46 nonsense mutation 46 hypoparathyroidism 46 ATTR PN 46 Myelofibrosis 46 chromosomal disorder 46 RDEB 46 Wilms tumor 46 Thyroid Cancer 46 Tay Sachs 46 cancer cachexia 46 acute myeloid leukemia AML 46 Colorectal Cancer 46 alopecia 46 FEVR 46 Gaucher disease 46 ZFP Therapeutic 46 Bladder Cancer 46 inoperable pancreatic cancer 46 Wegener granulomatosis 46 cardiac hypertrophy 46 Pancreas Cancer 46 non hodgkin lymphoma 46 peripheral arterial disease 46 von Willebrand Disease 46 Lewy Body 46 Sandhoff disease 46 degenerative nerve disorder 46 rhabdomyosarcoma rare 46 Myelodysplastic syndrome 46 Vasculitis Foundation 46 Brain Tumour Research 46 hematologic disorders 46 DiGeorge syndrome 46 cardiomyopathy weakening 46 Tay Sachs Disease 46 Obstructive Sleep Apnoea 46 iron overload 46 familial hypercholesterolemia 46 muscular dystrophies 46 non Hodgkins Lymphoma 46 Meningitis 46 Neurological Disorder 46 Malignant Mesothelioma 46 debilitating diseases 46 recurrent glioblastoma 46 Duchenne muscular dystrophy Duchenne 46 malignant melanoma 46 Pelizaeus Merzbacher disease 46 FRAXA Research 46 cystic kidney 46 Ewings sarcoma 46 Wilm tumor 46 Prostrate cancer 46 genetic defect 46 non hodgkins lymphoma 46 Rett syndrome neurological disorder 46 Spinal Cord Injuries 46 NF1 46 Krabbe leukodystrophy 46 Behcet uveitis 46 Ewing sarcoma bone 46 Hereditary angioedema 46 Essential Tremor 46 related macular degeneration 46 Usher syndrome 46 Schizophrenia 46 nephrotic syndrome 46 MS 46 Sarcoidosis 46 pulmonary hypertension PH 46 Cutaneous T 46 Fibrodysplasia 46 blastoma 46 chronic myelogenous leukemia 46 National Alopecia Areata 46 Aspergers Syndrome 46 Stroke NINDS 46 Parkinson disease neurodegenerative disorder 45 acute leukemias 45 Rheumatoid arthritis 45 T Cell Lymphoma 45 1 antitrypsin deficiency 45 preventable blindness 45 Cystic Fibrosis Trust 45 rare autosomal recessive 45 primary immunodeficiency 45 rheumatic diseases 45 Frontotemporal Dementia 45 lymphoma leukemia 45 Cerebral malaria 45 Fighting Blindness 45 Congenital Heart Disease 45 Tourette Syndrome 45 tuberous sclerosis 45 melanoma 45 neuroendocrine cancer 45 PAOD 45 retinal dystrophies 45 preventions treatments 45 Ulcerative colitis 45 progressive neurodegenerative 45 acute leukemia 45 genetic neuromuscular disorder 45 membranous nephropathy 45 prostrate cancer 45 Tumor Foundation 45 Tourette Syndrome TS 45 myelodysplastic syndrome 45 Urea Cycle Disorders 45 Stem Cell Transplant 45 brain malformation 45 MODY 45 Bowel Cancer 45 gastrointestinal stromal tumor GIST 45 Crohn disease chronic 45 diseases 45 retinoblastoma rare 45 Short Stature 45 Augie Quest 45 Sjogren Syndrome 45 gene therapy 45 acute myelocytic leukemia 45 PNH 45 Li Fraumeni syndrome 45 leukemia lymphoma 45 birth defects premature 45 IPF 45 pancreatic cancer 45 Synovial Sarcoma 45 breast cancer 45 FRAXA 45 Scoliosis 45 Motor neurone disease 45 Non Hodgkins lymphoma 45 Hepatocellular Carcinoma HCC 45 HER2 positive breast cancer 45 prostate cancer 45 SJIA 45 PIDD 45 CdLS 45 ADPKD 45 Alzheimers 45 pulmonary fungal infections 45 ARVD 45 myelodysplasia 45 Alport syndrome 45 Autism Spectrum Disorder 45 Investigational Treatment 45 heterozygous FH 45 autism neurological disorder 45 Myelodysplastic syndromes MDS 45 myelogenous leukemia 45 progressive degenerative neurological 45 Myelodysplastic Syndromes 45 Glioblastoma multiforme GBM 45 chronic lymphocytic leukemia CLL 45 homozygous familial hypercholesterolemia 45 Sjögren Syndrome 45 metastasized melanoma 45 motor neurone disease 45 chordoma 45 spinal cord injuries 45 Reflex Sympathetic Dystrophy RSD 45 Psoriatic arthritis 45 Spinal Cord 45 Neovascular Age Related Macular 45 skeletal muscle weakness 45 Lymphoma Research 45 Autism Spectrum Disorder ASD 45 Kufs disease 45 brain tumor 45 intractable epilepsy 45 metastatic prostate cancer 45 hepatitis C viral infection 45 diffuse pontine glioma 45 dysautonomia 45 progressive neuromuscular 45 Paroxysmal Nocturnal Hemoglobinuria PNH 45 xeroderma pigmentosum 45 hepatocellular carcinoma 45 muscle degeneration 45 Artificial Pancreas 45 atypical hemolytic uremic syndrome 45 hereditary deafness 45 respiratory viral infections 45 PTLD 45 illness variant Creutzfeldt 45 idiopathic thrombocytopenic purpura 45 Aicardi syndrome 45 Hutchinson Gilford progeria 45 Lennox Gastaut Syndrome 45 systemic juvenile idiopathic 45 eosinophilic asthma 45 dystrophy 45 Scleroderma Research 45 progressive neurological disorder 45 Catena ® 45 B Cell Lymphoma 45 Leukaemia Research 45 Retinitis pigmentosa 45 antibody MAb 45 neuro muscular disorder 45 immuno inflammatory diseases 45 lymphoma 45 Crohn Colitis 45 Kidney Disease 45 FoldRx 45 Autoimmune Diseases 45 hereditary disorders 45 Hereditary angioedema HAE 45 diabetic nephropathy 45 Meningiomas 45 inflammatory bowel diseases 45 HeFH 45 basal cell carcinoma BCC 45 Sickle cell 45 tetrabenazine 45 genetic syndromes 45 debilitating neurological disease 45 Neurological Diseases 45 Cachexia 45 ulcerative colitis 45 HAE 45 systemic mastocytosis 45 Camp Kemo 45 Acute lymphoblastic leukemia 45 Alopecia 45 Dravet 45 Alzheimer Dementia 45 chronic myeloid leukemia CML 45 biliary atresia 45 Shwachman Diamond Syndrome 45 Friedreich 45 Parkinson 45 Astrocytoma 45 PDGFRA 45 Angioedema 45 familial ALS 45 pigmentosa 45 variable immunodeficiency 45 Montel Williams MS 45 VCFS 45 chorea associated 45 neurological disorder affecting 45 2 diabetes T2D 45 acute lymphocytic leukemia 45 Anemia 45 Aryplase 45 Glycogen Storage Disease 45 Cockayne syndrome 45 onset diabetes 45 Idiopathic Pulmonary Fibrosis IPF 44 acute leukemia AML 44 Brain Aneurysm Foundation 44 Laminitis 44 autosomal recessive disease 44 arthritis 44 Factor VIIa 44 Multiple sclerosis 44 Islet Transplantation 44 Ehlers Danlos 44 Systemic Juvenile Idiopathic 44 Chagas disease 44 Vitiligo 44 Nonalcoholic Fatty Liver Disease 44 Noonan Syndrome 44 non alcoholic steatohepatitis 44 myositis 44 Leukaemia CARE 44 recurrent glioblastoma multiforme 44 Hypoparathyroidism 44 Disease 44 autism 44 Female Sexual Arousal 44 Follicular lymphoma 44 primary lateral sclerosis 44 Liver Cancer 44 Depression NARSAD 44 acromegaly 44 Arrhythmogenic Right Ventricular Cardiomyopathy 44 intermittent claudication 44 ADA SCID 44 autism spectrum disorders 44 Diabetic Retinopathy 44 amyloidosis 44 Trisomy 44 simplex virus 44 Li Fraumeni Syndrome 44 eosinophilic esophagitis 44 Deep Vein Thrombosis DVT 44 pulmonary arterial hypertension 44 Fx #A 44 Fanconi Anaemia 44 fibrodysplasia ossificans progressiva FOP 44 Vasculitis 44 degenerative retinal diseases 44 debilitating neurodegenerative 44 Tuberous sclerosis 44 RLS 44 Tay Sachs disease 44 Focal Segmental Glomerulosclerosis 44 ovarian cancer 44 Friedreich Ataxia Research 44 congenital heart 44 chronic myeloid 44 bilateral retinoblastoma 44 degenerative neurological diseases 44 Pediatric Brain Tumors 44 SCD 44 immune thrombocytopenic purpura ITP 44 Parkinson Disease PD 44 bowel cancer 44 Wet AMD 44 Janus kinase 44 acute intermittent porphyria 44 Apert Syndrome 44 diseases afflicting 44 relapsing remitting multiple sclerosis 44 cachexia 44 chronic renal failure 44 Staphylococcus aureus infections 44 Wiskott Aldrich syndrome 44 Guillain Barré Syndrome 44 Canine Cancer 44 Fanconi anemia rare 44 Niemann Pick Type 44 retinal degeneration 44 sporadic ALS 44 Peutz Jeghers syndrome 44 inherited metabolic disorders 44 colorectal cancer 44 diabetic kidney 44 mitochondrial disorders 44 gastric lymphoma 44 relapsing remitting 44 Wellcome Trust Case 44 juvenile dermatomyositis 44 exon skipping 44 Rare Diseases 44 Neurofibromatosis Type 44 nasopharyngeal carcinoma 44 IRSF 44 aspergers syndrome 44 Neuropathy 44 Li Fraumeni 44 stem glioma 44 Multiple Myeloma MM 44 liposomal ciprofloxacin 44 Coronary Heart Disease 44 homozygous FH 44 juvenile idiopathic arthritis 44 spastic paraplegia 44 Compassionate Care ALS 44 CLL 44 antiphospholipid syndrome APS 44 Symadex 44 Hirschsprung Disease 44 Clubfoot 44 syringomyelia 44 pediatric acute lymphoblastic 44 Testicular cancer 44 macular disease 44 ataxia telangiectasia AT 44 Alagille syndrome 44 myeloproliferative disease 44 Colon Cancer 44 FOLOTYN ® 44 metastatic cancer 44 DebRA charity 44 Adrenal Cancer 44 von Willebrand disease 44 leading charitable funder 44 juvenile myoclonic epilepsy 44 Fibromyalgia Syndrome 44 cystic fibrosis sufferers 44 Rett Syndrome Research 44 erythematosus 44 Acute leukemia 44 Feline Leukemia Virus 44 subependymal giant cell 44 Ocular Immunology 44 growth hormone deficiency 44 MDA Augie Quest 44 atypical rhabdoid tumor 44 Liver Disease 44 vWD 44 Chronic Lymphocytic Leukemia CLL 44 SMARTRISK 44 Osteogenesis Imperfecta 44 Zavesca 44 hypertrophic cardiomyopathy HCM 44 Muscle Function 44 alcoholic hepatitis