Related by context. All words. (Click for frequent words.) 75 Duchenne Muscular Dystrophy 72 muscular dystrophy 72 Duchenne 69 Duchenne muscular dystrophy DMD 65 Friedreich ataxia 65 Duchenne Muscular Dystrophy DMD 64 cystic fibrosis 63 Muscular dystrophy 62 genetic disorder 62 Angelman Syndrome 62 neuroblastoma 61 cystic fibrosis CF 61 Spinal Muscular Atrophy SMA 61 Spinal Muscular Atrophy 61 neuromuscular disease 61 degenerative disorder 61 Becker muscular dystrophy 60 mitochondrial disease 60 spinal muscular atrophy SMA 60 amyotrophic lateral sclerosis ALS 60 limb girdle muscular dystrophy 60 spinal muscular atrophy 60 juvenile diabetes 59 Rett syndrome 59 ALS 59 Fanconi anemia 59 Pompe disease rare 59 Rett Syndrome 59 acute myeloid leukemia 59 Muscular Dystrophy 58 Friedreich Ataxia 58 muscle wasting 58 myasthenia gravis 58 neurodegenerative disease 58 fatal neurodegenerative disorder 58 Leber congenital amaurosis 58 fatal neurodegenerative 58 Neuroblastoma 58 hypophosphatasia 58 myotonic dystrophy 57 degenerative neurological disorder 57 Pompe Disease 57 Pompe disease 57 rhabdomyosarcoma 57 Angelman syndrome 57 Hurler syndrome 57 neurofibromatosis 57 inherited neurodegenerative disorder 57 Sanfilippo Syndrome 57 Huntington Disease 57 multiple sclerosis 57 fatal neuromuscular disorder 57 leukemia 57 Leber Congenital Amaurosis LCA 57 Fragile X syndrome 57 Osteosarcoma 56 neurodegenerative disorder 56 Leber Congenital Amaurosis 56 motor neuron disease 56 leukodystrophies 56 polycystic kidney disease 56 Hutchinson Gilford Progeria Syndrome 56 Stargardt disease 56 Ewing Sarcoma 56 Cystic Fibrosis 56 Amyotrophic Lateral Sclerosis ALS 56 Polycystic Kidney Disease 56 acute lymphoblastic leukemia 56 Fragile X Syndrome 56 chronic granulomatous disease 55 Batten Disease 55 Krabbe disease 55 neurological disorder 55 Niemann Pick disease 55 debilitating autoimmune 55 myelofibrosis 55 Ewing sarcoma 55 ALS Amyotrophic Lateral Sclerosis 55 Progeria 55 Rhabdomyosarcoma 55 epidermolysis bullosa 55 mitochondrial diseases 55 Krabbe Disease 55 cerebral palsy 55 Pompe 55 NF2 54 metabolic disorder 54 congenital muscular dystrophy 54 cystinosis 54 juvenile myelomonocytic leukemia 54 Usher Syndrome 54 Crohn disease 54 chromosome abnormality 54 autoimmune disease 54 Cystic Fibrosis CF 54 progressive neurological disorder 54 Sanfilippo syndrome 54 Cystic fibrosis 54 progressive neurodegenerative disorder 54 Leber congenital amaurosis LCA 54 progeria 54 PTC# 54 MPS VI 54 degenerative neuromuscular disease 54 motor neuron diseases 54 Duchene muscular dystrophy 54 dyskeratosis congenita 54 leukemia ALL 54 osteosarcoma 54 Neurofibromatosis 54 Hutchinson Gilford progeria 54 Canavan Disease 54 Duchene Muscular Dystrophy 54 sickle cell disease 53 lymphoblastic leukemia 53 Multiple Sclerosis 53 Acute Myelogenous Leukemia 53 Dravet syndrome 53 dystonia 53 Acute Lymphoblastic Leukemia 53 lupus 53 Lou Gehrigs disease 53 Juvenile Rheumatoid Arthritis 53 idiopathic pulmonary fibrosis IPF 53 Mitochondrial Disease 53 Parkinson disease 53 Cystinosis 53 lysosomal storage diseases 53 Hurler Syndrome 53 Fragile X 53 cerebal palsy 53 neuromuscular disorders 53 histiocytosis 53 Amyotrophic lateral sclerosis 53 epilepsy 53 acute myelogenous leukemia AML 53 Myasthenia gravis 53 Acute Myelogenous Leukemia AML 53 autism 53 juvenile rheumatoid arthritis 53 inherited retinal degeneration 53 AAT deficiency 53 RDEB 53 nonsense mutation 53 Myotonic dystrophy 53 Lafora disease 53 mitochondrial myopathy 53 spinocerebellar ataxia 53 degenerative neurological disease 53 Leukemia 53 ependymoma 53 osteosarcoma bone 53 Retinitis Pigmentosa RP 52 degenerative disease 52 carcinoid cancer 52 scleroderma 52 muscular dystrophies 52 Scleroderma 52 Duchenne Becker 52 Fanconi Anemia 52 hereditary blindness 52 RPE# 52 DiGeorge syndrome 52 Polycystic kidney disease 52 dystrophy 52 medulloblastoma 52 tuberous sclerosis complex 52 Stargardt Macular Dystrophy 52 Maroteaux Lamy syndrome 52 Cerebral palsy 52 Burkitt lymphoma 52 retinitis pigmentosa 52 genetic defect 52 Ataxia 52 Burkitt Lymphoma 52 systemic scleroderma 52 hereditary spastic paraplegia 52 Juvenile Diabetes 52 incurable neurological disorder 52 immunodeficiency disease 52 osteogenesis imperfecta 52 genetic disorders 52 ectodermal dysplasia 52 multiple myeloma 52 lymphoblastic lymphoma 52 Hemophilia B 52 Dystonia 52 amyloidosis 52 Morquio syndrome 51 infantile spasms 51 degenerative muscular 51 Retinoblastoma 51 Dravet Syndrome 51 epidermolysis bullosa EB 51 hemophagocytic lymphohistiocytosis 51 Parkinson Disease 51 autism neurological disorder 51 neuronal ceroid lipofuscinosis NCL 51 spastic diplegia 51 neuroendocrine tumors 51 incurable neurodegenerative disease 51 MELAS 51 Acute Leukemia 51 multiple sclerosis MS 51 rheumatoid arthritis 51 degenerative neurological condition 51 ceroid lipofuscinosis NCL 51 neuromuscular disorder 51 Leukodystrophy 51 Nephrotic Syndrome 51 FSHD 51 Wiskott Aldrich Syndrome 51 degenerative nerve disorder 51 inherited neurological disorder 51 Hodgkin Lymphoma 51 hereditary disorder 51 progressive neurodegenerative disease 51 Glioblastoma 51 acute myelogenous leukemia 51 aplastic anemia 51 Krabbe Leukodystrophy 51 adrenoleukodystrophy ALD 51 neuro degenerative disorder 51 Parkinsons disease 51 Lou Gehrig Disease 51 synovial sarcoma 51 retinal degeneration 51 Rhabdomyosarcoma rare 51 incurable disease 51 lymphocytic leukemia 51 inflammatory arthritis 51 Hutchinson Gilford Progeria 51 Ewings Sarcoma 51 Cushing Syndrome 51 NPHP 51 FSGS 51 progeria rare 51 Leber Hereditary Optic Neuropathy 51 Tuberous Sclerosis 51 facioscapulohumeral muscular dystrophy 51 Lou Gherig disease 51 acute myeloid leukemia AML 50 ataluren 50 Alport Syndrome 50 pulmonary arterial hypertension 50 neurofibromatosis NF 50 debilitating neurological disorder 50 mitochondrial disorder 50 Hereditary angioedema HAE 50 disease 50 DMD 50 Parkinson degenerative 50 Hodgkins lymphoma 50 neuromuscular diseases 50 DIPG 50 Wilms tumor 50 lupus nephritis 50 sarcoma 50 skeletal muscle weakness 50 Alport syndrome 50 amyotrophic lateral sclerosis 50 Histiocytosis 50 Prader Willi Syndrome 50 wet macular degeneration 50 chromosomal disorder 50 embryonal rhabdomyosarcoma 50 primary immunodeficiencies 50 Mucopolysaccharidosis 50 Battens Disease 50 inherited neurodegenerative 50 Amyotrophic lateral sclerosis ALS 50 Multiple Sclerosis MS 50 Lennox Gastaut syndrome 50 neurological diseases 50 mitochondrial disorders 50 multiple endocrine neoplasia 50 septo optic dysplasia 50 Niemann Pick 50 ataxia telangiectasia 50 cancer 50 Acute Myeloid Leukemia 50 Barth Syndrome 50 Medulloblastoma 50 rare neurological disorder 50 Alzheimer disease AD 50 myotonic muscular dystrophy 50 Alzheimers disease 50 Acute myeloid leukemia 50 muscular dystrophy cystic fibrosis 50 incurable genetic 50 Friedrich Ataxia 50 LHON 50 Crohn 50 Diamond Blackfan Anemia 50 sickle cell anemia 50 DBMD 50 Marfan Syndrome 50 retinal dystrophies 50 juvenile dermatomyositis 50 exon skipping 50 brain malformation 50 relapsed leukemia 50 dilated cardiomyopathy 50 Spinal muscular atrophy 50 autism spectrum disorders 50 sporadic ALS 50 Coeliac disease 49 neuropsychiatric disorder 49 Lou Gehrig disease 49 spinal cord injuries 49 retinitis pigmentosa RP 49 Maroteaux Lamy Syndrome 49 Sandhoff disease 49 CIDP 49 Glioblastoma multiforme GBM 49 cystic fibrosis hereditary 49 Pulmonary arterial hypertension 49 Krabbe leukodystrophy 49 retinoblastoma 49 alveolar rhabdomyosarcoma 49 myeloproliferative neoplasms 49 retinal diseases 49 myelodysplastic syndrome 49 fibrodysplasia ossificans progressiva FOP 49 leukemia AML 49 1 diabetes T1D 49 Tourette syndrome 49 Ewing sarcoma rare 49 genetic abnormality 49 primary immunodeficiency 49 pneumococcal meningitis 49 autoinflammatory diseases 49 diffuse intrinsic pontine glioma 49 Acute Myeloid Leukaemia AML 49 Chronic lymphocytic leukemia 49 hemophilia 49 Motor Neurone Disease 49 Lateral Sclerosis 49 Gaucher disease 49 hereditary degenerative 49 Aplastic Anemia 49 Brugada Syndrome 49 Crohn Disease 49 Severe Primary IGFD 49 Von Willebrand disease 49 AAT Deficiency 49 progressive degeneration 49 idiopathic pulmonary fibrosis 49 chronic myeloid 49 syringomyelia 49 Tay Sachs disease 49 myasthenia gravis MG 49 Acute Lymphocytic Leukemia 49 Diamond Blackfan anemia 49 retinal degenerative disease 49 hepatoblastoma 49 Pulmonary fibrosis 49 pulmonary hypertension 49 Fabry disease 49 lysosomal storage disease 49 Myelodysplastic syndrome 49 chronic myeloid leukemia 49 rheumatic disease 49 Stargardt Disease 49 spina bifida 49 Usher syndrome 49 ankylosing spondylitis 49 chronic lymphocytic leukemia 49 acute promyelocytic leukemia 49 osteogenic sarcoma 49 Parkinson disease neurodegenerative disorder 49 arthrogryposis 49 psoriatic arthritis 49 xeroderma pigmentosum 48 Morquio Syndrome 48 Pelizaeus Merzbacher disease 48 genetic neuromuscular disorder 48 Autism Spectrum Disorders 48 retinal degenerative diseases 48 progressive neuromuscular 48 neurodegenerative 48 spastic paraplegia 48 autosomal dominant 48 acute lymphocytic leukemia 48 DiGeorge Syndrome 48 fibrotic disease 48 degenerative neurological diseases 48 spinal cord injury 48 Charcot Marie Tooth 48 PKD 48 glioblastoma 48 Motor neurone disease 48 ataxia 48 gene therapy 48 fatal neuromuscular 48 medulloblastoma malignant brain tumor 48 Parkinsons Disease 48 muscle degeneration 48 psoriasis psoriatic arthritis 48 Diffuse Intrinsic Pontine Glioma 48 TTR amyloidosis 48 Idiopathic Pulmonary Fibrosis IPF 48 Epidermolysis Bullosa EB 48 metastatic melanoma 48 fronto temporal dementia 48 Aplastic anemia 48 non metastatic osteosarcoma 48 Proteus Syndrome 48 Rubinstein Taybi syndrome 48 Lymphoma 48 Exon Skipping 48 chordoma 48 1 antitrypsin deficiency 48 neurofibromatosis type 48 severe aplastic anemia 48 Autism 48 Neurofibromatosis type 48 Chronic Lymphocytic Leukemia 48 ATTR PN 48 Adrenoleukodystrophy 48 Trisomy 48 chromosomal defect 48 Glioblastoma Multiforme 48 Fabry Disease 48 Alzheimer disease 48 neurodegenerative diseases 48 Aicardi syndrome 48 homozygous familial hypercholesterolemia 48 Wilm Tumor 48 neurodegenerative disorders 48 achondroplasia 48 juvenile idiopathic arthritis JIA 48 Hodgkins Lymphoma 48 Dystrophy 48 intermittent claudication 48 systemic lupus erythematosus SLE 48 sarcomas 48 Tourette Syndrome TS 48 Down syndrome 48 Cardiomyopathy 48 myositis 48 dystrophin gene 48 beta thalassemia 48 Lou Gerhig disease 48 MPGN 48 Fanconi Anaemia 48 mitochondrial dysfunction 48 Wilms Tumor 48 Von Hippel Lindau 48 Congenital Muscular Dystrophy 48 Alzheimer Disease 48 Parkinsons 48 Wiskott Aldrich syndrome 48 atypical hemolytic uremic syndrome 48 rhabdomyosarcoma rare 48 inherited metabolic disorders 48 von Willebrand disease 48 inflammatory demyelinating 47 hematologic disorders 47 chronic myelogenous leukemia CML 47 pediatric brain tumor 47 juvenile idiopathic arthritis 47 RNAi therapeutic targeting 47 systemic lupus erythematosus 47 debilitating neuromuscular 47 chronic myeloid leukemia CML 47 mutated gene 47 medulloblastomas 47 HIBM 47 alzheimer disease 47 PKD Foundation 47 congenital blindness 47 Aicardi Syndrome 47 autosomal recessive 47 AA amyloidosis 47 neuro degenerative disease 47 Morquio 47 Crohns disease 47 debilitating diseases 47 nonsense mutations 47 ZFP Therapeutic 47 CHARGE syndrome 47 congenital disorder 47 Lou Gherig Disease 47 Acute Myeloid Leukemia AML 47 progressive neurodegenerative 47 autoimmune disorder 47 Acute Lymphoblastic Leukaemia 47 Epilepsy 47 Kufs disease 47 fatal myelination disorder 47 metastatic prostate cancer 47 vWD 47 Myocarditis 47 Fibrosis 47 metastatic colon cancer 47 metastatic cancer 47 eosinophilic esophagitis 47 neurobiological disorder 47 CFS ME 47 cardiomyopathy weakening 47 Multiple sclerosis 47 relapsing remitting 47 Infantile spasms 47 Retinitis pigmentosa 47 Myelodysplastic syndromes MDS 47 related macular degeneration 47 discoid lupus 47 Fragile X. 47 neurogenic orthostatic hypotension 47 cardiac hypertrophy 47 motor neurone 47 protein dystrophin 47 Severe Combined Immunodeficiency 47 leukodystrophy 47 neurological disorder affecting 47 achromatopsia 47 Hemochromatosis 47 Inflammatory Bowel Disease 47 leukemia CLL 47 chronic lymphocytic leukemia CLL 47 Leukemia Lymphoma 47 incurable hereditary 47 Lupus 47 Cockayne Syndrome 47 NF1 47 hereditary deafness 47 Rett syndrome neurological disorder 47 neurodevelopmental disorder 47 VCFS 47 seizure disorders 47 Acute lymphoblastic leukemia 47 secretory diarrhea 47 cystic kidney 47 inoperable pancreatic cancer 47 acute leukemia 47 myelodysplasia 47 smoldering myeloma 47 degenerative nerve 47 lymphoma 47 vasculitis 47 ataxia telangiectasia AT 47 Sudden Arrhythmia Death 47 Juvenile Idiopathic Arthritis JIA 47 Acute lymphocytic leukemia 47 CureDuchenne 47 preventions treatments 47 adrenoleukodystrophy 47 hemophilia B. 47 Meckel Gruber 47 inflammatory bowel diseases 47 glioblastoma multiforme GBM 46 erythematosus 46 immunodeficiency disorder 46 pseudotumor cerebri 46 prion diseases 46 ADPKD 46 Stapled Peptide 46 Joubert Syndrome 46 autism spectrum disorder 46 diffuse pontine glioma 46 Hirschsprung disease 46 primary lateral sclerosis 46 Cerebral Palsy 46 Autoimmune diseases 46 osteogenesis imperfecta OI 46 acute leukemias 46 chiari malformation 46 familial hypercholesterolemia 46 Tuberous sclerosis 46 haemophilia 46 Parkinson disease neurological disorder 46 neurodevelopmental disorders 46 Alzhiemer 46 Joubert syndrome 46 hematological malignancy 46 cancer cachexia 46 Fanconi anemia FA 46 Cushing syndrome 46 lateral sclerosis ALS 46 enzyme deficiency 46 Cystic fibrosis CF 46 blood clotting disorder 46 PIDD 46 Angelman 46 tuberous sclerosis 46 neuro muscular disorder 46 degenerative diseases 46 debilitating neurodegenerative 46 AML Leukemia 46 scoliosis 46 common disabling neurological 46 late infantile neuronal 46 optic nerve hypoplasia 46 Non Hodgkins lymphoma 46 untreatable diseases 46 familial ALS 46 multisystem disease 46 spinocerebellar ataxia type 46 1 Antitrypsin Deficiency 46 biliary atresia 46 Cockayne syndrome 46 Crigler Najjar syndrome 46 autistic 46 developmental disorder 46 acute myelogenous 46 Autism Spectrum Disorder ASD 46 diseases 46 iron overload 46 neuroblastomas 46 cachexia 46 Ewing Sarcoma rare 46 ALS amyotrophic lateral sclerosis 46 Peutz Jeghers syndrome 46 sarcopenia 46 oligodendrogliomas 46 SOD1 46 autoimmune 46 neuro developmental disorder 46 nasopharyngeal carcinoma 46 neuroendocrine cancer 46 huntingtin gene 46 Stargardt macular dystrophy 46 non alcoholic steatohepatitis 46 nephrotic syndrome 46 prion disease 46 genetic syndromes 46 disease Molluscum Contagiosum 46 renal diseases 46 mucopolysaccharidosis 46 recessive dystrophic epidermolysis bullosa 46 primary pulmonary hypertension 46 Juvenile Arthritis 46 fatal neurodegenerative disorders 46 immuno inflammatory diseases 46 transverse myelitis 46 Reflex Sympathetic Dystrophy RSD 46 Rheumatoid arthritis 46 Prion diseases 46 Synovial Sarcoma 46 neurofibromatosis genetic disorder 46 Multiple sclerosis MS 46 arthritis 46 Wilms Tumour 46 Aortic stenosis 46 hypereosinophilic syndrome 46 Langerhans Cell Histiocytosis 46 LRRK2 gene 46 Aspergers Syndrome 46 Chronic myeloid leukemia 46 Cytomegalovirus 46 lysosomal storage disorders 46 Tay Sachs 46 Alzheimers Disease 46 rheumatic diseases 46 CdLS 46 Spina Bifida 46 Fanconi anemia rare 46 rhabdomyosarcoma rare cancer 46 Niemann Pick Disease 46 Chiari malformation 46 ankylosing spondylitis AS 46 myelodysplastic syndrome MDS 46 Apert Syndrome 46 Chronic Lymphocytic Leukemia CLL 46 cardiomyopathy 46 myeloproliferative disease 46 developmental disorders 46 Epstein Barr Virus 46 GM1 gangliosidosis 46 degenerative retinal diseases 46 Alopecia Areata 46 myelodysplastic syndromes 46 eosinophilic asthma 46 essential thrombocythemia 46 arthrogryposis multiplex congenita 46 deacetylase inhibitors 46 Cystic Fibrosis Foundation 46 progressive degenerative 46 pediatric sarcoma 46 Ectodermal Dysplasia 46 herpes zoster virus 46 Alzheimer 46 Acute Myeloid Leukaemia 46 Amyloidosis 46 Cachexia 46 hypoparathyroidism 46 inflammatory bowel disease 46 intractable epilepsy 46 brain tumors 46 Parkinson Disease PD 46 Parkinson disease PD 46 hereditary hemochromatosis 46 relapsing multiple sclerosis 46 Chronic Myeloid Leukemia 46 congenital deafness 46 Psoriatic arthritis 46 Familial Adenomatous Polyposis FAP 46 progressive supranuclear palsy 45 Marfan syndrome 45 degenerative disorders 45 Leukaemia 45 neurological disorders 45 PKU genetic 45 diabetic retinopathy DR 45 gastrointestinal stromal tumor 45 Pulmonary hypertension 45 kidney disease 45 polyneuropathy CIDP 45 hereditary disorders 45 leukemia lymphoma 45 Restless Legs Syndrome 45 inherited retinal 45 non Hodgkin Lymphoma 45 gene mutation 45 Sudden Unexplained Death 45 SNT-MC#/idebenone 45 neuroblastoma tumor 45 systemic amyloidosis 45 Pemphigus 45 Non Hodgkins Lymphoma 45 Systemic lupus 45 Klinefelter syndrome 45 Prostrate cancer 45 frontotemporal dementia 45 holoprosencephaly 45 mycosis fungoides 45 Proteus syndrome 45 HGPS 45 HeFH 45 RLS 45 Gaucher Disease 45 myeloma 45 Leber hereditary optic neuropathy 45 Philadelphia Chromosome Positive 45 relapsing remitting multiple sclerosis 45 neuropathies 45 Macular Degeneration 45 lymphangioleiomyomatosis LAM 45 defective gene 45 Down syndrome chromosomal disorder 45 chronic autoimmune disorder 45 Janus kinase 45 Non Hodgkin Lymphoma 45 pulmonary fibrosis PF 45 blastoma 45 Myelofibrosis 45 visilizumab 45 motor neuron degeneration 45 heterozygous FH 45 Parkinson disease degenerative 45 Major depressive disorder 45 Myopathy 45 Osteogenesis Imperfecta 45 Essential tremor 45 Parkinsonism 45 diabetic kidney 45 Myeloma 45 Myositis 45 dysautonomia 45 prostate cancer 45 Autoimmune disorders 45 Downs Syndrome 45 Loeys Dietz syndrome 45 idiopathic thrombocytopenic purpura ITP 45 hematological diseases 45 ANCA associated 45 autosomal recessive disorder 45 disabling neurological 45 progressive degenerative neurological 45 AA Amyloidosis 45 diabetic nephropathy 45 ALS Lou Gehrig 45 acute lymphatic leukemia 45 Multiple Myeloma Research 45 Sleeping sickness 45 illness variant Creutzfeldt 45 neurodegeneration 45 acute lymphoblastic 45 nonalcoholic cirrhosis 45 Ataxia Telangiectasia 45 chronic renal failure 45 Primary Immune Deficiency 45 Wolf Hirschhorn 45 liver disease 45 Tuberous Sclerosis Complex 45 Crohn disease chronic 45 cystic fibrosis Duchenne muscular 45 T1DM 45 interstitial lung disease 45 degenerative neurological 45 Idiopathic Pulmonary Fibrosis 45 Cholangiocarcinoma 45 autosomal recessive disease 45 Langerhans cell histiocytosis 45 Li Fraumeni 45 Follicular lymphoma 45 severe malignant osteopetrosis 45 genetic lysosomal storage 45 familial amyloidotic polyneuropathy FAP 45 lymphatic cancer 45 Atopic eczema 45 gynecological cancers 45 Acute Promyelocytic Leukemia 45 chronic myelogenous leukemia 45 malignant melanoma 45 Alagille syndrome 45 Multiple Myeloma 45 autosomal recessive genetic 45 myalgic encephalomyelitis ME 45 metastatic lung cancer 45 non Hodgkins lymphoma 45 pneumococcal infections 45 FTLD 45 metastatic osteosarcoma 45 Mitochondrial diseases 45 kidney urologic 45 Waldenstrom macroglobulinemia 45 Myelodysplastic syndromes 45 Cancer cachexia 45 homozygous FH 45 demyelinating diseases 45 astrocytoma 45 simplex virus 45 Hepatocellular Carcinoma HCC 45 Neurofibromatosis Type 45 JMML 45 Epidermolysis Bullosa 45 Ilaris 45 Periodontal disease 45 Stargardt Macular Dystrophy SMD 45 chronic autoimmune 45 variable immunodeficiency 45 Essential Tremor 45 neuro muscular diseases 45 antibody MAb 45 non hodgkin lymphoma 45 hemolytic anemia 45 chorea 45 neurogenetic 45 idiopathic thrombocytopenic purpura 45 cytomegalovirus CMV 45 autoimmune hemolytic anemia 45 gastrointestinal stromal tumors 44 Spina bifida 44 diabetes 44 Scoliosis 44 congenital adrenal hyperplasia CAH 44 Glioma 44 Macular degeneration 44 dilated cardiomyopathy DCM 44 Parkinson's 44 ulcerative colitis 44 retinoblastoma rare 44 Biliary Atresia 44 fungal meningitis 44 myelogenous leukemia 44 autism spectrum 44 chromosomal anomaly 44 Carcinoid tumors 44 quadriplegic cerebral palsy 44 Idiopathic Thrombocytopenic Purpura ITP 44 carcinoid 44 Mantle Cell Lymphoma 44 Brain Tumor 44 Ichthyosis 44 Eosinophilic 44 hormonal disorder 44 Bronchiectasis 44 Spinal cord injury 44 Cerebral malaria 44 transplanted bone marrow 44 postoperative ileus 44 diabetic neuropathy 44 immune mediated 44 acute leukemia AML 44 chronic neurological disorder 44 leiomyosarcoma 44 Prader Willi syndrome 44 protein misfolding diseases 44 Pancreatic Cancer 44 Hodgkin lymphoma HL 44 Sickle cell 44 Lennox Gastaut Syndrome 44 Aviptadil 44 Hodgkin Disease 44 onset Alzheimer disease 44 systemic mastocytosis 44 spastic quadriplegic cerebral palsy 44 Inflammatory bowel disease 44 Pneumococcal meningitis 44 congenital hyperinsulinism 44 Pervasive Developmental Disorder 44 PAOD 44 immunodeficiency 44 GVHD 44 pigmentosa 44 cardiac channelopathies 44 paroxysmal nocturnal hemoglobinuria PNH 44 Lateral Sclerosis ALS 44 degenerative nerve disease 44 Infantile Spasms 44 autoimmune uveitis 44 haematological cancers 44 Neovascular Age Related Macular 44 Creutzfeldt Jakob disease 44 dyspraxia 44 breast cancer metastasis 44 pulmonary hypertension PH 44 mastocytosis 44 Guillian Barre syndrome 44 macular degeneration diabetic retinopathy 44 Wegener granulomatosis 44 acromegaly 44 pemphigus vulgaris 44 recurrent glioblastoma multiforme 44 renal cell carcinoma 44 dyskinetic 44 ARVD 44 HER2 positive breast cancer 44 systemic lupus 44 Peripheral neuropathy 44 Non Hodgkin lymphoma 44 Aplastic Anaemia 44 non Hodgkin lymphoma 44 Ankylosing spondylitis 44 MODY 44 retinitis pigmentosa macular degeneration 44 aplastic anemia rare 44 Kaposi sarcoma 44 familial adenomatous polyposis 44 Primary IGFD 44 Pulmonary Fibrosis 44 Autistic Disorder 44 systemic juvenile idiopathic 44 bilateral retinoblastoma 44 CLL 44 Pulmonary Hypertension 44 debilitating neurological disease 44 pancreatic cancer 44 Adenoid Cystic Carcinoma 44 ichthyosis 44 nephritis 44 Arthritis 44 sleeping sickness 44 FTIs 44 interstitial pulmonary fibrosis 44 Metastatic breast cancer 44 FMR1 gene 44 Amyotrophic Lateral Sclerosis 44 macular degeneration 44 osteopetrosis 44 alopecia 44 dwarfism 44 HQK 44 LQTS 44 pontine glioma 44 remyelination 44 Melanoma 44 Chronic Inflammatory Demyelinating Polyneuropathy 44 Osteoarthritis OA 44 diseases fat malabsorption 44 RNAi therapeutics 44 pulmonary fibrosis 44 autism spectrum disorders ASDs 44 acute myeloid 44 craniosynostosis 44 commercialize deforolimus 44 recessive genetic 44 refractory gout 44 ACV1 44 Wet AMD 44 autoimmune encephalitis 44 peripheral arterial disease 44 tetrabenazine 44 Multiple myeloma 44 autoimmune diseases 44 Ulcerative colitis 44 PPMD 44 Testicular cancer 44 neurologic diseases 44 phenylketonuria 44 retrovirus 44 macular disease 44 dimentia 44 Osteoarthritis 44 minimally symptomatic 44 urological cancers 44 generalized epilepsy 44 sickle cell 44 pancreatic islet cell 44 Ehlers Danlos syndrome 44 retinitis pigmentosa degenerative 44 Cogane 44 muscular dystrophy cerebral palsy 44 chromosome #q#.# deletion 44 Glioblastoma multiforme 44 immune thrombocytopenic purpura ITP 44 McCune Albright